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Which Startups Will Present at HLTH?

MedCity News

The post Which Startups Will Present at HLTH? Startups will take part in four different competitions at HLTH. There will also be plenty of opportunities to network. appeared first on MedCity News.

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Vertex presents longer-term data that shows durability and consistency of Casgevy

Fierce Pharma

Six months after Vertex earned a historic FDA approval for sickle cell d | Six months after Vertex earned a historic FDA approval for sickle cell disease (SCD) gene therapy Casgevy (exa-cel), long-term data is beginning to show the consistent efficacy and durability of the treatment, which is the first ever to be developed using CRISPR gene editing (..)

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Medical Sales Presentations: Be Brief, Add Value

MedReps

Few things are as important as sales presentations for someone working in medical sales. Since the goal is to get your customers and clients to purchase the items you’re selling, these presentations are the best methods of informing them about your products, as well as pointing out how those products solve a problem.

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Microbial risks presented by aging facilities

European Pharmaceutical Review

In an article published in the Journal of Validation Technology (JVT), pharmaceutical microbiologist and contamination control expert Tim Sandle identified ten categories of risk presented by aging. Degradation of the facilities, for instance cracks in walls or tears in material, can also present contamination challenges.

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Roadblocks to Delivering a Competitive Buying Experience

Buyers struggle with being overwhelmed, indecision, and trusting the information that’s presented to them. Today’s buying experience is extremely challenging to navigate––with a plethora of choices, easy access to research, and competing (often contradictory) voices chiming in. For a buyer-facing team, the struggle is also real.

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Data for First-in-Class IV-Administered Gene Therapy to Treat Epilepsy Presented at ASGCT 2024

PharmaTech

The company is presenting preclinical data at the American Society of Gene & Cell Therapy annual meeting that supports the potential of the company’s CAP-002 gene therapy for correcting neurological phenotypes associated with genetic epilepsy due to syntaxin-binding protein 1 (STXBP1) mutations.

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Gene therapy for rare muscular dystrophy presents preliminary promise

European Pharmaceutical Review

At present, there are no curative treatments for LGMD2I/R9. Additionally, these first results were also presented at the 2023 International Limb-Girdle Muscular Dystrophy Conference. According to Atamyo Therapeutics, the condition is characterised by progressive muscular weakness, leading to loss of the ability to walk independently.